0:00 3:40 Introduction
3:41 53:37 Presentation
53:38 1:04:00 Q&A
1:04:01 1:05:59 Conclusion

Dr. Don Kohn of UCLA provides an update on emerging gene therapy treatments for ADASCID.

The information, terminology, and opinions presented in this forum do not necessarily reflect the views of IDF, its Board of Trustees, sponsors, or donors.

Presented with support from Chiesi Global Rare Diseases.